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GILBERT FAMILY FOUNDATION'S GENE THERAPY INITIATIVE, LLC (GTI)
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Research
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Exon Skipping to Treat NF1
Exploring Nonsense Suppression as a Treatment for NF1
NF1 Experimental Mouse Models: Histopathology and Neuroanatomical Phenotyping
NF1 Gene Rescue in Translational Animal Models
NF1 Gene Rescue in Translational Animal Models
NF1 RNA Repair Based on Therapeutic Ribozymes
Targeted Delivery of Full Length NF1 cDNA using Non-viral Vectors