Taking Stock of Retinal Gene Therapy: Looking Back and Moving Forward

Academic Article


  • Over the past 20 years, there has been tremendous progress in retinal gene therapy. The safety and efficacy results in one early-onset severe blinding disease may lead to the first gene therapy drug approval in the United States. Here, we review how far the field has come over the past two decades and speculate on the directions that the field will take in the future.
  • Authors

    Published In

  • Molecular Therapy  Journal
  • Digital Object Identifier (doi)

    Author List

  • Bennett J
  • Start Page

  • 1076
  • End Page

  • 1094
  • Volume

  • 25
  • Issue

  • 5