Molecular Therapy - Methods and Clinical Development

Journal

Overview
Identity

Publication Venue For

Safety of Same-Eye Subretinal Sequential Readministration of AAV2-hRPE65v2 in Non-human Primates. 15:133-148. 2019

CRISPR Activation Enhances In Vitro Potency of AAV Vectors Driven by Tissue-Specific Promoters. 13:380-389. 2019

An Adeno-Associated Viral Vector Capable of Penetrating the Mucus Barrier to Inhaled Gene Therapy. 9:296-304. 2018

Modeling Anti-HIV-1 HSPC-Based Gene Therapy in Humanized Mice Previously Infected with HIV-1. 9:23-32. 2018

Corrigendum to “Efficient gene delivery to photoreceptors using AAV2/rh10 and rescue of the Rho–/– mouse” (Molecular Therapy - Methods and Clinical Development (2015) 2 (S2329050116300286) (10.1038/mtm.2015.16)). 3:16032. 2016

Efficient gene delivery to photoreceptors using AAV2/rh10 and rescue of the Rho^−/− mouse. 2:15016. 2015

Electronic International Standard Serial Number (eissn)

2329-0501